2 US Girls Become World's First To Get Gene Therapy For Genetic Brain Disorder

2 US girls become world's first to get gene therapy for 'Rett syndrome' in girls

A team of US doctors have in a world first delivered a novel gene therapy to treat Rett syndrome -- a rare genetic brain disorder -- in two girls. They became the first children worldwide to receive the promising treatment as part of the first-in-human Phase I/II trial of a new investigational gene therapy, NGN-401, developed by US-based Neurogene. Dec 4, 2023
Thymalin

Thymalin Research in Immune System Function

Thymalin is the synthetic version of Thymulin isolated from the thymus in 1977. Thymalin has been speculated to regulate inflammation and pain, may have neuroprotective impact, and may be important in immune function Nov 24, 2023